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ISTH 2019 – Quality of Life of Hemophilia Patients with Inhibitors – Opportunities for Improvement
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AAV Based Hemophilia B Gene Therapy in Mice Using FIX-CB2679d-GT
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ISTH 2019 – Phase 2/3 Trial of Subcutaneous Engineered FVIIa Marzeptacog Alfa (Activated) in Hemophilia A or B with Inhibitors: Efficacy, Safety and Pharmacokinetics
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